Exon Skipping technology is an innovative new therapeutic platform that treats a specific mutation of Duchenne Muscular Dystrophy. Patients and caregivers were not aware of or did not understand the concept of Exon Skipping or the benefits.

The website includes an Exon Mapping Tool to help explain exon deletions and skips and how they may be linked to treatment. The output informs visitors that there is a current therapy being studied with the possibility of future therapies becoming available.

With minimal promotion, SkipAhead.com resulted in more than 700 rare DMD enrollees. 50 potential trial participants were identified in the first 3 months.